My goal is to be like everyone else
and to have them forget my disability

Mandine

Patient Stories

Thumbnail of Mandine, a patient with calpainopathy (LGMDR1)
Mandine

Patient with Calpainopathy (LGMD-R1)

“My goal is to be like everyone else and to have them forget my disability.”

View video
Apollo

Patient with γ-sarcoglycanopathy (LGMD-R5)

“I see myself as a warrior. Not a warrior who fights on the field, but someone who fights a mental battle.”

View story
Jonas

Patient with Calpainopathy (LGMD-R1)

“Strangely enough, I have more and more faith in treatment.”

View video
Johann

Patient with α-Sarcoglycanopathy (LGMD-R3)

“My life is frail, but I want it to be full, I don't want it to be ordinary, I want it to be extraordinary.”

View story

To find out more about our clinical trials please contact us.